Tippi MacKenzie (left), MD, of UCSF Benioff Children’s Hospital San Francisco, visits with newborn Elianna, who received a stem cell transplant before birth. Photo by Barbara Ries
Note: The consortium brings together UC's five medical center campuses — Davis, Irvine, Los Angeles, San Diego and San Francisco — to share resources and expertise to help develop new drugs.
To develop a new drug, or create a new diagnostic test or medical device, a scientist often needs a catalyst – something to spark the innovative idea that has the potential to change the way a disease is treated and improve patient outcomes.
When a child is diagnosed with a rare and life-threatening disease, the parents often don’t know where to turn.
Mark Dant was told his toddler, Ryan, wouldn’t make it to his tenth birthday. Ryan had a rare genetic disorder, the doctors called it, Mucopolysaccharidosis (MPS I).